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Ramu Gopalappa ... In-Jeoung Baek*, and Hyongbum Henry Kim*
In Vivo Adenine Base Editing Rescues Adrenoleukodystrophy in a Humanized Mouse Model
Mol. Ther.
Date: May 24, 2024
Link:
https://doi.org/10.1016/j.ymthe.2024.05.027
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